GeneticsbioRxivPreprint
Selective Disruption of Mutant TP63 Alleles Restores Corneal Epithelial proliferation in EEC Syndrome
Giulia Masi, Gualtiero Alvisi, Patrizia Nespeca…·Marta Trevisan
This study uses CRISPR/Cas9 to disrupt mutant TP63 alleles in patient-derived cells, improving corneal epithelial proliferation in EEC syndrome.
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