NeurosciencebioRxivPreprint
Optimization of microRNA Target Sequence Arrangement in AAV Vectors Dramatically Enhances Specificity and Efficiency of Transgene Expression in Cortical Microglia
Ryo Aoki, Ayumu Konno, Nobutake Hosoi…·Hirokazu Hirai
This paper develops an AAV vector system with optimized miR.Ts placement to achieve specific and efficient transgene expression in microglia.
DOI 10.1101/2024.11.05.622037