PathologyMolecular TherapyPeer-reviewed
Truncated Complement Factor H Y402 Gene Therapy Cures C3 Glomerulonephritis
Lindsey A. Chew, Daniel Grigsby, C. Garren Hester…·Catherine Bowes Rickman
This study shows that AAV-delivered truncated CFH gene therapy can reverse C3G in mice and suggests its potential for treating AMD.
3 citations