Molecular BiologybioRxivPreprint
Efficient and accurate prime editing strategy to correct genetic alterations in hiPSC using single EF-1alpha driven all-in-one plasmids
Wout J. Weuring, Nina Dirkx, Els De Vriendt…·Bobby P.C. Koeleman
This study develops and tests novel all-in-one plasmids for prime editing in hiPSC, achieving up to 50% edit efficiency with reduced off-target effects.
3 citations