NeuroscienceNeuroscience BulletinPeer-reviewed
Co-editing PINK1 and DJ-1 genes via AAV-delivered CRISPR/Cas9 system in adult monkey brains elicits classic Parkinsonian phenotypes
Hao Li, Shihao Wu, Xia Ma…·Xintian Hu
This study edits PINK1 and DJ-1 genes in adult monkey brains using AAV-delivered CRISPR/Cas9, resulting in Parkinsonian symptoms and pathology.
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