Molecular BiologyMolecular Therapy — Nucleic AcidsPeer-reviewed
Exon-Skipping Antisense Oligonucleotides for H3.3K27M-Altered Diffuse Midline Glioma Therapy
Lucia Yang, Qian Zhang, John Erby Wilkinson…·Adrian R. Krainer
This study demonstrates that exon-skipping antisense oligonucleotides targeting H3.3K27M-altered DMG reduce proliferation and extend survival in a mouse model.
DOI 10.1016/j.omtn.2026.103040