GeneticsbioRxivPreprint
Single anticodon-edited tRNA therapy targeting highly prevalent Arg>Ter premature termination codons causing inherited retinal diseases
Asodu Sandeep Sarma, A Saleh, Jonathan Eintracht…·Dror Sharon
This paper develops a single therapeutic molecule targeting the most common class of nonsense variants in inherited retinal diseases using anticodon-edited tRNA.
DOI 10.64898/2026.07.21.737205