GeneticsbioRxivPreprint
Therapeutic adenine base editing corrects nonsense mutation and improves visual function in a mouse model of Leber congenital amaurosis
Dong Hyun Jo, Hyeon‐Ki Jang, Chang Sik Cho…·Jeong Hun Kim
This study uses adenine base editing to correct a nonsense mutation in a mouse model of LCA, improving visual function.
12 citations