Molecular BiologybioRxivPreprint
A New Approach to Modeling LGMDR1: Pyrvinium-Treated capn3b crispant Zebrafish
Cristina Ruiz‐Roldán, Andrea Valls, Jenita Immanuel…·Amets Sáenz
The paper develops a pharmacologically enhanced zebrafish model of LGMDR1 by treating capn3b mutants with pyrvinium, mimicking human gene expression patterns and highlighting Wnt pathway involvement.
DOI 10.1101/2025.11.25.690358