Pharmacology & ToxicologybioRxivPreprint
Lipid-ASO therapeutics exhibit differential tissue targeted delivery upon systemic or local CNS administration
Samantha Roudi, Hernando Yesid Estupiñan, Osama Saher…·Samir EL Andaloussi
This study compares lipid-conjugated ASO delivery in mice, showing differential tissue and CNS targeting based on lipid type and administration route.