A novel porcine model of CLN3 Batten disease recapitulates clinical phenotypes
Vicki J. Swier, Katherine A. White, Tyler B. Johnson, Xiaojun Wang, Jimin Han, David A. Pearce, Ruchira Singh, Arlene V. Drack, Wanda L. Pfeifer, Christopher S. Rogers, Jon J. Brudvig, Jill M. Weimer
This paper presents a novel porcine model of CLN3 Batten disease that recapitulates clinical phenotypes observed in humans.
Disease Models & Mechanisms · Jun 12, 2023Peer-reviewedNeuroscience