Novel Strategy against AML by Rescuing Loss of Phase Separation of Pathogenic NPM1c
Yuting Zhu, Weifan Xu, Rong Wang, Lijuan Hu, Xiao‐Jun Huang, Hong-Hu Zhu, Pilong Li
This study identifies a small molecule that rescues NPM1c phase separation loss, restoring nucleolar localization and showing anti-leukemia activity in AML models.
bioRxiv · Apr 8, 2025 · PreprintCancer Biology