NeurosciencebioRxivPreprint
Efficient in vivo mammalian neuron editing using peptide-mediated CRISPR enzyme delivery
Brigette D. Manohar, Meika Travis, Vikas Munjal…·Ross C. Wilson
This study develops Neuro-PERC, a peptide-mediated CRISPR delivery method, enabling efficient in vivo neuronal editing in mice and pigs, and extending survival in a Huntington's disease model.