NeuroscienceFrontiers in NeurosciencePeer-reviewed
Gene editing preserves visual function in a mouse model of retinal degeneration
Paola Vagni, Laura E. Perlini, Naïg Aurélia Ludmilla Chenais…·Diego Ghezzi
This study uses CRISPR/Cas9 gene editing in a mouse model of retinal degeneration to preserve visual function, showing improved acuity and preserved light responses.
38 citations