BiochemistrybioRxivPreprint
High Throughput Screening Identifies a Small Molecule Trafficking Corrector for Long-QT Syndrome Associated KCNQ1 Variants
Katherine R. Clowes, Carlos G. Vanoye, Ana Cristina Chang-Gonzalez…·Charles R. Sanders
This study identifies a small molecule, VU0494372, that enhances KCNQ1 expression and trafficking, offering a potential therapeutic approach for LQTS.
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