Expanded CAG/CTG Repeats Resist Gene Silencing Mediated by Targeted Epigenome Editing
Bin Yang, Alicia C. Borgeaud, Marcela Buřičová, Lorène Aeschbach, Oscar Rodríguez‐Lima, Gustavo A. Ruiz Buendía, Cinzia Cinesi, Alysha S Taylor, Tuncay Baubec, Vincent Dion
The paper develops a system to study how expanded CAG/CTG repeats affect gene silencing via epigenome editing and finds that repeats reduce silencing effectiveness.
Human Molecular Genetics · Sep 7, 2021Peer-reviewedMolecular Biology