Overcoming the effect of ASH1L haploinsufficiency on stem cells amenability to genome editing and differentiation into the neuronal lineage - a technical report
Seon Hye Cheon, Foster D. Ritchie, Janay M. Vacharasin, Nicholas A. Marinelli, Collin Cheatle, Mikayla M. McCord, Kaitlin Cox, Sofia B. Lizarraga
This paper describes protocols to overcome ASH1L haploinsufficiency in stem cells, improving genome editing and neuronal differentiation efficiency.
bioRxiv · Sep 27, 2021 · PreprintNeuroscience