Molecular BiologyNAR Molecular MedicinePeer-reviewed
Systematic deletion of symmetrical CFTR exons reveals new therapeutic targets for exon skipping antisense oligonucleotides
Cecilia Peña‐Rasgado, Elvia Rodriguez-Manriquez, Miroslav Dundr…·Wren E. Michaels
This study identifies therapeutic targets for exon skipping antisense oligonucleotides by systematically analyzing CFTR isoforms generated through symmetrical exon deletion.
2 citations