Multiplex Epigenome Editing of MECP2 to Rescue Rett Syndrome Neurons
J. Qian, X. Guan, B. Xie, C. Xu, J. Niu, X. Tang, C. Li, H. Colecraft, R. Jaenisch, X. S. Liu
This study uses multiplex epigenome editing to reactivate MECP2 from the inactive X chromosome in RTT neurons, rescuing neuronal defects in vitro.
bioRxiv · Nov 30, 2022 · PreprintPhysiology