Human cellular model systems of β-thalassemia enablein-depth analysis of disease phenotype
D. E. Daniels, I. Ferrer-Vicens, J. Hawksworth, T. N. Andrienko, E. M. Finnie, D. C. J. Ferguson, A. S. F. Oliveira, J.-Y. A. Szeto, M. C. Wilson, J. Frayne
This study creates human cellular models of β-thalassemia to analyze disease phenotype and develops an assay to assess treatment responses.
bioRxiv · Sep 1, 2022Cell Biology