AAV vectors with enhancer-controlled ITR promoters
Yanjiang Zheng, Luzi Yang, Kaiyu Zhou, Qirun Wang, Tiange Li, Jiahao Wu, Jiangwei Qin, Fei Gao, Pingzhu Zhou, Tian Lu, Yangpo Cao, Yimin Hua, Yuxuan Guo, Yifei Li
This paper designs AAV vectors with enhancer-controlled ITR promoters to improve payload capacity and enable tissue-specific gene editing with a single AAV.
bioRxiv · Dec 5, 2025 · PreprintBioengineering