Inhibition of NLRP1 Inflammasome Activation by Tyrosine Kinase Inhibitors Restores Erythropoiesis in Diamond-Blackfan Anemia Syndrome
Juan M. Lozano Gil, Lola Rodríguez‐Ruiz, Manuel Palacios, Jorge Peral, Susana Navarro, José Luís Fuster, Cristina Beléndez, Andrés Jerez, Laura Murillo, Cristina Díaz de Heredia, Guzmán López-de-Hontanar, Josune Zubicaray, Julián Sevilla, Francisca Ferrer‐Marín, María P. Sepulcre, , Víctoriano Mulero
This study shows that tyrosine kinase inhibitors can restore erythropoiesis in Diamond-Blackfan Anemia by inhibiting NLRP1 inflammasome activation.
bioRxiv · Feb 20, 2025 · PreprintImmunology