Impaired oligodendrocyte maturation is an early feature in SCA3 disease pathogenesis
Kristen H. Schuster, Annie J. Zalon, Hongjiu Zhang, Danielle M. DiFranco, Nicholas R. Stec, Zaid Haque, Kate G. Blumenstein, Amanda M. Pierce, Yuanfang Guan, Henry Lauris Paulson, Hayley S. McLoughlin
This study identifies impaired oligodendrocyte maturation as an early feature in SCA3 disease pathogenesis through longitudinal transcriptomic analysis and functional validation in mice.
Journal of Neuroscience · Jan 18, 2022Peer-reviewedNeuroscience