Acetyl-Leucine slows disease progression in lysosomal storage disorders
Ecem Kaya, David Aitchison Smith, Claire Smith, Lauren Morris, Tatiana Brémovà-Ertl, Mario Cortina‐Borja, Paul Fineran, Karl Morten, Joanna Poulton, Barry Boland, John Spencer, Michael Leo Strupp, Frances M. Platt
This study shows that ADLL and its enantiomer ALL slow disease progression in lysosomal storage disorders through mechanisms involving glucose and antioxidant metabolism.
Brain Communications · Sep 15, 2020Peer-reviewedNeuroscience