Establishment of a second-generation transgenic marmoset model of polyglutamine disease recapitulating neurological symptoms and pathology
Eiko Nakano Minakawa, Kensuke Owari, Naotake Nogami, Terumi Nakatani, Masashi Koizumi, Akiyo Kawanobe, Yosuke Saga, Moeko Kudo, S. Noguchi, Takashi Hanakawa, Yuki Hori, Hidemi Numazawa, Toshihide Takeuchi, Yuko Katakai, Ryoichi Saito, , Kazuhiko Seki
This paper describes a second-generation transgenic marmoset model of SCA3 that replicates motor impairments and neuropathology, offering a platform for studying disease mechanisms and therapies.
bioRxiv · Mar 12, 2025 · PreprintNeuroscience