NeuroscienceeLifePeer-reviewed
Human HPSE2 gene transfer ameliorates bladder pathophysiology in a mutant mouse model of urofacial syndrome.
Filipa M. Lopes, Céline Grenier, Benjamin W. Jarvis…·Neil A. Roberts
This paper demonstrates that AAV-mediated HPSE2 gene transfer improves bladder function in a mouse model of urofacial syndrome by restoring neurogenic relaxation.
1 citation