CRISPR-pass: Gene rescue of nonsense mutations using adenine base editors
Choongil Lee, Dong Hyun Jo, Gue‐Ho Hwang, Jihyeon Yu, Jin‐Soo Kim, Se-eun Park, Jeong Hun Kim, Sangsu Bae
CRISPR-pass uses adenine base editors to bypass nonsense mutations in patient-derived fibroblasts, showing potential for treating genetic disorders.
Molecular Therapy · May 23, 2019Peer-reviewedMolecular Biology