NeurosciencebioRxiv
Efficient in vivo neuronal genome editing in the mouse brain using nanocapsules containing CRISPR-Cas9 ribonucleoproteins
Jeanette M. Metzger, Yuyuan Wang, Samuel S. Neuman…·Shaoqin Gong
This study develops non-viral nanocapsules for in vivo CRISPR-Cas9 delivery to edit neuronal DNA in mice, achieving efficient and safe genome editing in specific neuron types.
34 citations