NeurosciencebioRxivPreprint
Inhibition of VCP preserves retinal structure and function in autosomal dominant retinal degeneration
Blanca Arango‐González, Merve Sen, Rosellina Guarascio…·Marius Ueffing
This study shows that inhibiting VCP activity rescues degenerating P23H rod cells and improves their function in retinal models of adRP.