NeuroscienceMolecular Therapy — Methods & Clinical DevelopmentPeer-reviewed
SMALL ALPHAHERPESVIRUS LATENCY-ASSOCIATED PROMOTERS DRIVE EFFICIENT AND LONG-TERM TRANSGENE EXPRESSION IN THE CENTRAL NERVOUS SYSTEM
Carola J. Maturana, Jessica L. Verpeut, Thomas John Pisano…·Esteban A. Engel
The paper identifies small herpesvirus latency-associated promoters that enable long-term, pan-neuronal transgene expression in the CNS using AAV vectors.
20 citations