Cancer BiologybioRxivPreprint
Cholesterol Biosynthesis is a Targetable Vulnerability of CEBPA-mutant Acute Myeloid Leukemia
Sofie Ulfbeck Schovsbo, Yang Liu, Pedro Aragon-Fernandez…·Bo Torben Porse
This study identifies cholesterol biosynthesis as a therapeutic target in CEBPA-mutant AML, showing that statins enhance chemosensitivity in cells with co-mutations in TET2 or WT1.