BioengineeringbioRxivPreprint
Beyond the Cut: Long-read sequencing reveals complex genomic and transcriptomic changes in AAV-CRISPR therapy for Duchenne Muscular Dystrophy
Mary S. Jia, Made Harumi Padmaswari, Landon A. Burcham…·Christopher E. Nelson
This study uses long-read sequencing to analyze genomic and transcriptomic changes in AAV-CRISPR therapy for DMD, revealing complex editing outcomes and developing new methods for detection.
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