GeneticsbioRxivPreprint
A Dual-Locus-Targeting Strategy to Enhance CRISPR/Cas9-mediated CFTR Replacement via Helper-Dependent Adenoviral vector in porcine genome
Z Chen, Zhichang Peter Zhou, Rongqi Cathleen Duan…·Jim Hu
The paper develops a dual-locus-targeting strategy using CRISPR/Cas9 and helper-dependent adenoviral vectors to improve CFTR gene replacement in porcine cells.
DOI 10.64898/2026.06.10.731381