BioinformaticsbioRxivPreprint
A chemoinformatics-guided platform for efficient discovery of RNA-binding small molecules: Proof-of-concept for myotonic dystrophy type 1
Amirhossein Taghavi, Jingsong Shan, Xiyuan Yao…·Matthew David Disney
The paper develops a chemoinformatics platform to discover RNA-binding small molecules, identifying ligands for the r(CUG)exp RNA in DM1 with splicing rescue activity.
DOI 10.64898/2026.05.08.723748