BioengineeringbioRxivPreprint
Engineering Human ARMMs as Therapeutic Non-Viral Vehicles for in vivo Delivery of Genome Editing Payloads
Qiyu Wang, Shu-Lin Liu, Wen‐Ning Zhao…·Joseph F. Nabhan
This paper engineers human-derived ARMMs for in vivo delivery of genome editing tools, showing efficient gene knockout and therapeutic potential in mouse models.