Engineering Human ARMMs as Therapeutic Non-Viral Vehicles for in vivo Delivery of Genome Editing Payloads
Qiyu Wang, Shu-Lin Liu, Wen‐Ning Zhao, Ryan A. von Kleeck, Michael G. Thomas, Kristin M. Luther, Zahra Vahramian, Yumei Sun, Komal Vyas, Pearl Moharil, Chris Chatzinakos, Carson Semple, Jennifer A Badji, Leah Gens, Alysia Bryant, , Joseph F. Nabhan
This paper engineers human-derived ARMMs for in vivo delivery of genome editing tools, showing efficient gene knockout and therapeutic potential in mouse models.
bioRxiv · Sep 24, 2024 · PreprintBioengineering