BioengineeringbioRxivPreprint
Curative levels of endogenous gene replacement achieved in non-human primate liver using programmable genomic integration
Jenny Xie, Maike Thamsen Dunyak, Patrick Hanna…·Jonathan D. Finn
This paper demonstrates programmable genomic integration in non-human primate liver, achieving curative levels of gene expression in over 50% of liver cells.