PhysiologybioRxivPreprint
Prevenying vision loss in a mouse model of Leber Congenital Amaurosis by engineered tRNA
Enes Akyüz, Pawan Kumar Shahi, Lionel Gissot…·Bikash Ranjan Pattnaik
This study demonstrates that engineered tRNA can restore vision in a mouse model of Leber Congenital Amaurosis by suppressing a premature termination codon.
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