Pharmacology & ToxicologybioRxivPreprint
An aptamer targeting TfR1 enhances ASO delivery to muscle tissue
Matthew John Warner, Linsley Kelly, Reetu Thakur…·Matthew Levy
This study evaluates an aptamer targeting TfR1 for enhancing ASO delivery to muscle tissue, showing >50% target gene knockdown in mice for 42 days.
DOI 10.64898/2026.07.13.737509