NeuroscienceCell ReportsPeer-reviewed
Rac1 inhibition prevents axonal cytoskeleton dysfunction in Transthyretin Amyloid Polyneuropathy
Joana Magalhães, Vítor Pacheco Dias, Jessica Eira…·Márcia A. Liz
This study shows that Rac1 inhibition prevents cytoskeletal dysfunction in ATTRv-PN by rescuing axonal defects in mice and supporting its therapeutic potential in patients.
3 citations