Cell BiologybioRxivPreprint
In vivo gene disruption and homology-directed repair in muscles and muscle stem cells using CRISPR/Cas9
Bryan L. Peacker, Kuan‐Hung Lin, Amy Lam…·Amy J. Wagers
This study demonstrates CRISPR-HDR efficiency in postnatal cardiac, skeletal muscle, and muscle stem cells, showing developmental stage-dependent HDR rates and successful correction of a Dmd mutation in mdx mice.
DOI 10.64898/2026.06.30.735705