NeuroscienceProceedings of the National Academy of SciencesPeer-reviewed
The nuclear ubiquitin ligase adaptor SPOP is a conserved regulator of C9orf72 dipeptide toxicity
Carley Snoznik, Valentina Medvedeva, Jelena Mojsilovic‐Petrovic…·Todd Lamitina
This paper identifies SPOP as a conserved regulator of C9orf72 dipeptide toxicity in C. elegans and mammalian neurons, showing SPOP inhibition protects against toxicity.
11 citations