Citra Nurfarah Zaini Mattar

This study demonstrates the feasibility of using dual-ssAAV6 vectors for in vivo gene delivery to HSC from thalassemia patients in a humanized mouse model, showing efficient transduction and long-term persistence.

This paper develops an optimized digital PCR method for rapid, absolute quantification of DNA, RNA, and extracellular microRNA in mouse oocytes, demonstrating high accuracy and reproducibility.