Cell BiologybioRxivPreprint
Enhancement of Prednisolone efficacy and safety in Duchenne muscular dystrophy via neutrophil elastase inhibition
K.A. Johnson, Fiona K. Jones, Rachel S. Ghadiali…·A Pisconti
This paper shows that combining Alvelestat with Prednisolone improves muscle function and reduces side effects in a DMD mouse model.
DOI 10.1101/2025.02.26.640472