Cell BiologybioRxivPreprint
In utero and neonatal lipid nanoparticle delivery achieves robust editing in hematopoietic stem cells.
Atesh K. Worthington, Beltran Borges, Elisa Schrader Echeverri…·Tippi C. MacKenzie
This study demonstrates efficient in utero and neonatal lipid nanoparticle delivery for genome editing of hematopoietic stem cells, achieving robust editing and multilineage reconstitution.
2 citations