Cell BiologybioRxivPreprint
Genomic splice-donor disruption rescues systemic disease in progeria
Wei Zhu Jin, Jingchun Ma, Hao Yuan…·Zhongjun Zhou
This paper shows that disrupting a faulty splice donor site in progeria reduces toxic protein levels and extends lifespan in mice.
DOI 10.64898/2026.09.17.752274