ImmunologybioRxivPreprint
Complement inhibition by C3-siRNA treatment prevents AChR loss and reduces complement activation in the rat Passive Transfer Myasthenia Gravis (PTMG)
Anja Kristina Schöttler, Marina Mané-Damas, Britt Arets…·Pilar Martínez‐Martínez
C3-siRNA treatment in PTMG rats reduces AChR loss and MAC deposition, improving muscle function and suggesting complement inhibition as a therapeutic strategy for AChR-MG.
DOI 10.1101/2025.08.31.673367