Retinal organoids mirror CRISPR/Cas9 gene editing efficiency observed in vivo
Juliette Pulman, Hugo Malki, Paul Oudin, Ecem Aydin, Sophie Tran, Laura Visticot, Camille Robert, Anne De Cian, Marie As, Olivier Goureau, Jean‐Paul Concordet, Deniz Dalkara
The paper compares CRISPR/Cas9 gene editing efficiency in retinal organoids, HEK293T cells, and mouse models, finding retinal organoids better mirror in vivo editing outcomes.
Molecular Therapy — Methods & Clinical Development · Nov 11, 2025Peer-reviewedBioengineering