Rigosertib reverses hypertrophic cardiomyopathy in RAF1-associated Noonan syndrome
Levi Legler, Bing Xu, Tara Keshavarz Shirazi, Sereene Kurzum, Katya Marchetti, Chase W. Kessinger, Izabella Vredenburg, Yan Sun, Frank A. Dinenno, Damian Bohler, Angelika G. Aleman, Nelson A. Rodriguez, Simon Ng, Sophie Weiwei Gao, Angela Wang, , Maria Irene Kontaridis
This paper shows rigosertib reverses hypertrophic cardiomyopathy in RAF1-associated Noonan syndrome using Drosophila, iPSC, and mouse models.
bioRxiv · Nov 25, 2024 · PreprintMolecular Biology