Molecular BiologybioRxivPreprint
Rigosertib reverses hypertrophic cardiomyopathy in RAF1-associated Noonan syndrome
Levi Legler, Bing Xu, Tara Keshavarz Shirazi…·Maria Irene Kontaridis
This paper shows rigosertib reverses hypertrophic cardiomyopathy in RAF1-associated Noonan syndrome using Drosophila, iPSC, and mouse models.
DOI 10.1101/2024.11.25.623865